WHITE PAPER: Unleashing the potential of real-world evidence in rare diseases

Murthy A, Mantegazza R, Larkin M, Friconneau M, Annemans L, Van Damme B, Sokol T, Emond S (2022)

Recommendations for optimising the use, design and regulation of real-world evidence (RWE) collection based on an expert panel hosted by the Associazione Italiana Miastenia (AIM) on 1 March 2021.

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